We are focused on the development of precision genetic medicines to treat rare neuromuscular and central nervous system diseases. Learn more about Sarepta.

Sarepta is a global biotechnology company on an urgent mission: to engineer precision genetic medicine for rare diseases that devastate lives and cut futures short.

Read news and articles from Sarepta, a global biotechnology company developing potentially life-changing precision genetic medicine.

Apr 8, 2025 · Sarepta’s industry-leading pipeline is comprised of programs in various stages of development. Currently, Sarepta has one gene therapy and three RNA-based therapies on the …

At Sarepta, we are committed to living our cultural values; they are the guidepost for every action we take. If you are energized and inspired by the opportunity to toss aside convention and break down …

Advancing the promise of precision genetic medicine Sarepta is pursuing the development of precision genetic medicine at the forefront of biotechnology for rare diseases.

Sarepta is committed to creating breakthrough treatments for people whose lives are being cut short and burdened by rare diseases. Fundamental to that mission are carefully designed and conducted …

At Sarepta, we’re committed to pursuing some of the world’s most debilitating, prevalent, and complex rare genetic diseases. Learn more about the disease areas we're focused on.

Vyondys 53 website U.S. Full Prescribing Information (PDF) Amondys 45 website SareptAssist SareptAssist is a patient support program here to help on your treatment journey. Call 1-888 …

Sarepta is a proud sponsor of Decode Duchenne, a program of Parent Project Muscular Dystrophy that is administered by Duchenne Connect. Learn more about Decode Duchenne