Inherited retinal dystrophy (IRD) isn’t one disease. It’s many different ones that cause your retina to break down and stop working. They can make you color-blind or night blind. Others can lead to ...

Please provide your email address to receive an email when new articles are posted on . The loss of UBAP1L gene function appears to be associated with nonsyndromic retinal dystrophy, according to ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy ...

(RTTNews) - MeiraGTx Holdings Plc. (MGTX), a clinical-stage genetic medicines company, on Friday announced the progress in its gene therapy program for Leber Congenital Amaurosis 4 or LCA4, a severe ...

CHICAGO — Children with a rare, inherited retinal disorder who were treated with the first Food and Drug Administration-approved gene therapy had noticeable improvements in vision that may be related ...

This story is part of a series on the current progression in Regenerative Medicine. This piece is part of a series dedicated to the eye and improvements in restoring vision. In 1999, I defined ...

Finding showed patients treated with tinlarebant achieved a statistically significant 35.7% reduction in lesion growth rate vs placebo. Topline data were announced from a phase 3 trial evaluating ...

The Korea Research Institute of Standards and Science (KRISS, President Lee Ho Seong) has developed a retina-mimicking eye phantom* that faithfully replicates the structural layers and microvascular ...

ATLANTA, May 5, 2025 /PRNewswire/ -- Odylia Therapeutics, a nonprofit (501(c)3) biotechnology company dedicated to advancing treatments for rare diseases, today announced its latest pipeline project: ...